Cele mai recente publicații
Ex Vivo and In Vivo Gene Therapy for Mucopolysaccharidoses: State of the Art
Hematol Oncol Clin North Am. 2022 Aug;36(4):865-878.
Consiglieri G, Bernardo ME, Brunetti-Pierri N, Aiuti A.
Case Report: Consistent disease manifestations with a staggered time course in two identical twins affected by adenosine deaminase 2 deficiency
Front Immunol. 2022 Sep 29;13:910021.
Barzaghi F, Cicalese MP, Zoccolillo M, Brigida I, Barcella M, Merelli I, Sartirana C, Zanussi M, Calbi V, Bernardo ME, Tucci F, Migliavacca M, Giglio F, Doglio M, Canarutto D, Ferrua F, Consiglieri G, Prunotto G, Saettini F, Bonanomi S, Rovere-Querini P, Di Colo G, Jofra T, Fousteri G, Penco F, Gattorno M, Hershfield MS, Bongiovanni L, Ponzoni M, Marktel S, Milani R, Peccatori J, Ciceri F, Mortellaro A, Aiuti A.
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
MPSI Study Group. N Engl J Med. 2021 Nov 18;385(21):1929-1940.
Gentner B, Tucci F, Galimberti S, Fumagalli F, De Pellegrin M, Silvani P, Camesasca C, Pontesilli S, Darin S, Ciotti F, Sarzana M, Consiglieri G, Filisetti C, Forni G, Passerini L, Tomasoni D, Cesana D, Calabria A, Spinozzi G, Cicalese MP, Calbi V, Migliavacca M, Barzaghi F, Ferrua F, Gallo V, Miglietta S, Zonari E, Cheruku PS, Forni C, Facchini M, Corti A, Gabaldo M, Zancan S, Gasperini S, Rovelli A, Boelens JJ, Jones SA, Wynn R, Baldoli C, Montini E, Gregori S, Ciceri F, Valsecchi MG, la Marca G, Parini R, Naldini L, Aiuti A, Bernardo ME;
Evidence of Treatment Benefits in Patients with Mucopolysaccharidosis Type I-Hurler in Long-term Follow-up Using a New Magnetic Resonance Imaging Scoring System
J Pediatr. 2022 Jan;240:297-301.e5.
Pontesilli S, Baldoli C, Rosa PAD, Cattoni A, Bernardo ME, Meregalli P, Gasperini S, Motta S, Fumagalli F, Tucci F, Baciga F, Consiglieri G, Canonico F, De Lorenzo P, Chiapparini L, Gentner B, Aiuti A, Biondi A, Rovelli A, Parini R.
A Case of Two Adult Brothers with Wiskott-Aldrich Syndrome, One Treated with Gene Therapy and One with HLA-Identical Hematopoietic Stem Cell Transplantation
J Clin Immunol. 2021 Nov 4.
Consiglieri G, Ferrua F; San Raffaele Hospital Consortium, Aiuti A, Cicalese MP.
Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series
Mol Ther Methods Clin Dev. 2021 Jun 1;22:76-83.
Canarutto D, Tucci F, Gattillo S, Zambelli M, Calbi V, Gentner B, Ferrua F, Marktel S, Migliavacca M, Barzaghi F, Consiglieri G, Gallo V, Fumagalli F, Massariello P, Parisi C, Viarengo G, Albertazzi E, Silvani P, Milani R, Santoleri L, Ciceri F, Cicalese MP, Bernardo ME, Aiuti A.
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent β-thalassemia
Nature Medicine 25, 234-241 (2019).
Marktel S, Scaramuzza S, Cicalese MP, Giglio F, Galimberti S, Lidonnici MR, Calbi V, Assanelli A, Bernardo ME, Rossi C, Calabria A, Milani R, Gattillo S, Benedicenti F, Spinozzi G, Aprile A, Bergami A, Casiraghi M, Consiglieri G, Masera N, D’Angelo E, Mirra N, Origa R, Tartaglione I, Perrotta S, Winter R, Coppola M, Viarengo G, Santoleri L, Graziadei G, Gabaldo M, Valsecchi MG, Montini E, Naldini L, Cappellini MD, Ciceri F, Aiuti A, Ferrari G.
Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cel gene therapy
Bone Marrow Transplant. 2019 May 31.
Tucci F, Frittoli M, Barzaghi F, Calbi V, Migliavacca M, Ferrua F, Fumagalli F, Lorioli L, Castagnaro L, Facchini M, Fossati C, Zanzan S, Massariello P, Manfredini M, Consiglieri G, Canarutto D, Recupero S, Calzatini F, Casiraghi M, Darin S, Antonioli G, Miniero R, Fiori R, Silvani P, Zambelli M, Marktel S, Gattillo S, Milani R, Santoleri L, Ciceri F, Biffi A, Cicalese MP, Bernardo ME, Aiuti A.
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent β-thalassemia
Nature Medicine 25, 234-241 (2019).
Marktel S, Scaramuzza S, Cicalese MP, Giglio F, Galimberti S, Lidonnici MR, Calbi V, Assanelli A, Bernardo ME, Rossi C, Calabria A, Milani R, Gattillo S, Benedicenti F, Spinozzi G, Aprile A, Bergami A, Casiraghi M, Consiglieri G, Masera N, D’Angelo E, Mirra N, Origa R, Tartaglione I, Perrotta S, Winter R, Coppola M, Viarengo G, Santoleri L, Graziadei G, Gabaldo M, Valsecchi MG, Montini E, Naldini L, Cappellini MD, Ciceri F, Aiuti A, Ferrari G.
Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy
Bone Marrow Transplantation (2018) 53:913–917
Valeria Calbi, Francesca Fumagalli, Giulia Consiglieri, Rachele Penati, Serena Acquati, Daniela Redaelli, Vanessa Attanasio, Facchini Marcella, Maria Pia Cicalese, Maddalena Migliavacca, Federica Barzaghi, Francesca Ferrua, Andrea Assanelli, Paolo Silvani, Matteo Zoccolillo, Giovanna Chidini, Robert Chiesa, Ruchi Arora, Francesca Ciotti, Marina Sarzana, Gigliola Antonioli, Cristina Baldoli, Francesco Morena, Sabata Martino, Gian Luigi Ardissino, Maria Grazia Natali Sora, Luigi Naldini, Fabio Ciceri, Alessandro Aiuti, Maria Ester Bernardo.
Successful treatment with Harvoni® in an ADA-SCID infant with HCV infection allowed gene therapy with Strimvelis®
Epub July 16, 2018.
Francesca Tucci, Valeria Calbi, Federica Barzaghi, Maddalena Migliavacca, Francesca Ferrua, Maria Ester Bernardo, Daniele Canarutto, Giulia Consiglieri, Salvatore Recupero, Francesco Calzatini, Michela Gabaldo, Caterina Lucano, Miriam Casiraghi, Silvia Darin, Francesca Dionisio, Sarah Marktel, Enza Cestone, Renato Finazzi,Giorgina Mieli-Vergani, Enzo Boeri, Jonathan Appleby, Dalia Abd Elaziz, Fabio Ciceri, Alessandro Aiuti, Maria Pia Cicalese Hepatology.
Mild SARS-CoV-2 Infection after Gene Therapy in a child with Wiskott-Aldrich Syndrome: a case report
Frontiers in Immunology, November 2020 | Volume 11 | Article 603428
Sabina Cenciarelli, Valeria Calbi, Federica Barzaghi, Maria Ester Bernardo, Chiara Oltolini, Maddalena Migliavacca, Vera Gallo, Francesca Tucci, Federico Fraschetta, Elena Albertazzi, Elena Sophia Fratini, Giulia Consiglieri, Stefania Giannelli,Francesca Dionisio, Claudia Sartirana, Sara Racca, Chiara Camesasca, Giovanni Peretto, Rita Daverio, Antonio Esposito, Francesco De Cobelli, Paolo Silvani, Marco Rabusin, Andrea Cara, Daria Trabattoni, Stefania Dispinseri, Gabriella Scarlatti, Lorenzo Piemonti, Vito Lampasona, Maria Pia Cicalese, Alessandro Aiuti and Francesca Ferrua.
